Last Updated: Monday, November 18, 2013
Principal Investigator: John Phillips III, M.D.
"Peg Pal" (BMN 165) is a drug that has been shown to help in reducing blood Phe concentrations in patients with PKU.
We want to know more about:
For more information about this study, visit the clinicaltrials.gov website.
Adults over 16 to 70 with PKU
$50 per week and reimbursement for travel
varies between 8 and 16 visits
Anyone diagnosed with mucopolysaccharide storage disorder type 1 (MPS-1), Gaucher, Fabry, or Pompe diseaseCompensation: Yes
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